Early manifestations and differential gene expression associated with photoreceptor degeneration in prom1-deficient retina
(2021) In DMM Disease Models and Mechanisms 14(11). p.1-11- Abstract
Retinitis pigmentosa (RP) and macular dystrophy (MD) are characterized by gradual photoreceptor death in the retina and are often associated with genetic mutations, including those in the prominin-1 (Prom1) gene. Prom1-knockout (KO) mice recapitulate key features of these diseases including light-dependent retinal degeneration and constriction of retinal blood vessels. The mechanisms underlying such degeneration have remained unclear, however. We here analysed early events associated with retinal degeneration in Prom1-KO mice. We found that photoreceptor cell death and glial cell activation occur between 2 and 3 weeks after birth. Whereas gene expression was not affected at 2 weeks, the expression of several genes was altered at 3 weeks... (More)
Retinitis pigmentosa (RP) and macular dystrophy (MD) are characterized by gradual photoreceptor death in the retina and are often associated with genetic mutations, including those in the prominin-1 (Prom1) gene. Prom1-knockout (KO) mice recapitulate key features of these diseases including light-dependent retinal degeneration and constriction of retinal blood vessels. The mechanisms underlying such degeneration have remained unclear, however. We here analysed early events associated with retinal degeneration in Prom1-KO mice. We found that photoreceptor cell death and glial cell activation occur between 2 and 3 weeks after birth. Whereas gene expression was not affected at 2 weeks, the expression of several genes was altered at 3 weeks in the Prom1-KO retina, with the expression of that for endothelin-2 (Edn2) being markedly upregulated. Expression of Edn2 was also induced by light stimulation in Prom1-KO mice reared in the dark. Treatment with endothelin receptor antagonists attenuated photoreceptor cell death, gliosis and retinal vessel stenosis in Prom1-KO mice. Our findings thus reveal early manifestations of retinal degeneration in a model of RP/MD and suggest potential therapeutic agents for these diseases.
(Less)
- author
- publishing date
- 2021-11
- type
- Contribution to journal
- publication status
- published
- keywords
- Endothelin receptor antagonist, Endothelin-2, Glial cell, Photoreceptor, Prominin-1, Retinal degeneration
- in
- DMM Disease Models and Mechanisms
- volume
- 14
- issue
- 11
- article number
- dmm048962
- pages
- 1 - 11
- publisher
- The Company of Biologists Ltd
- external identifiers
-
- scopus:85121302935
- pmid:34664634
- ISSN
- 1754-8403
- DOI
- 10.1242/dmm.048962
- language
- English
- LU publication?
- no
- additional info
- Publisher Copyright: © 2021. Published by The Company of Biologists Ltd
- id
- 35f7bf59-5a24-44ca-a340-273528191c50
- date added to LUP
- 2026-01-23 23:28:33
- date last changed
- 2026-01-27 03:55:20
@article{35f7bf59-5a24-44ca-a340-273528191c50,
abstract = {{<p>Retinitis pigmentosa (RP) and macular dystrophy (MD) are characterized by gradual photoreceptor death in the retina and are often associated with genetic mutations, including those in the prominin-1 (Prom1) gene. Prom1-knockout (KO) mice recapitulate key features of these diseases including light-dependent retinal degeneration and constriction of retinal blood vessels. The mechanisms underlying such degeneration have remained unclear, however. We here analysed early events associated with retinal degeneration in Prom1-KO mice. We found that photoreceptor cell death and glial cell activation occur between 2 and 3 weeks after birth. Whereas gene expression was not affected at 2 weeks, the expression of several genes was altered at 3 weeks in the Prom1-KO retina, with the expression of that for endothelin-2 (Edn2) being markedly upregulated. Expression of Edn2 was also induced by light stimulation in Prom1-KO mice reared in the dark. Treatment with endothelin receptor antagonists attenuated photoreceptor cell death, gliosis and retinal vessel stenosis in Prom1-KO mice. Our findings thus reveal early manifestations of retinal degeneration in a model of RP/MD and suggest potential therapeutic agents for these diseases.</p>}},
author = {{Kobayashi, Yuka and Watanabe, Shizuka and Ong, Agnes Lee Chen and Shirai, Manabu and Yamashiro, Chiemi and Ogata, Tadahiko and Higashijima, Fumiaki and Yoshimoto, Takuya and Hayano, Takahide and Asai, Yoshiyuki and Sasai, Noriaki and Kimura, Kazuhiro}},
issn = {{1754-8403}},
keywords = {{Endothelin receptor antagonist; Endothelin-2; Glial cell; Photoreceptor; Prominin-1; Retinal degeneration}},
language = {{eng}},
number = {{11}},
pages = {{1--11}},
publisher = {{The Company of Biologists Ltd}},
series = {{DMM Disease Models and Mechanisms}},
title = {{Early manifestations and differential gene expression associated with photoreceptor degeneration in prom1-deficient retina}},
url = {{http://dx.doi.org/10.1242/dmm.048962}},
doi = {{10.1242/dmm.048962}},
volume = {{14}},
year = {{2021}},
}
