3-phosphoglycerate dehydrogenase deficiency : A case report of a treatable cause of seizures
(2009) In Turkish Journal of Pediatrics 51(6). p.587-592- Abstract
Serine deficiency disorders are a new group of neurometabolic diseases resulting from a deficiency in one of the three enzymes in the biosynthetic pathway of L-serine. Deficiency of the enzyme 3-phosphoglycerate dehydrogenase (3-PGDH), which catalyzes the first step in the biosynthetic pathway, leads to congenital microcephaly, severe psychomotor retardation, and intractable seizures. We report a 4 1/2-year-old boy who presented with congenital microcephaly, psychomotor retardation, hypertonia, strabismus, and drug-resistant seizures due to 3-PGDH deficiency. His seizures responded to L-serine and glycine supplementation only. This potentially treatable disease should be borne in mind in patients with congenital microcephaly,... (More)
Serine deficiency disorders are a new group of neurometabolic diseases resulting from a deficiency in one of the three enzymes in the biosynthetic pathway of L-serine. Deficiency of the enzyme 3-phosphoglycerate dehydrogenase (3-PGDH), which catalyzes the first step in the biosynthetic pathway, leads to congenital microcephaly, severe psychomotor retardation, and intractable seizures. We report a 4 1/2-year-old boy who presented with congenital microcephaly, psychomotor retardation, hypertonia, strabismus, and drug-resistant seizures due to 3-PGDH deficiency. His seizures responded to L-serine and glycine supplementation only. This potentially treatable disease should be borne in mind in patients with congenital microcephaly, psychomotor retardation and seizures. A timely diagnosis based on the detection of low cerebrospinal fluid levels of L-serine and glycine is expected to further increase the success of L-serine and glycine supplementation in these patients.
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- author
- Coşkun, Turgay ; Aydin, Halil Ibrahim ; Kiliç, Mustafa ; Dursun, Ali ; Haliloǧlu, Göknur ; Topaloǧlu, Haluk ; Karli-Oǧuz, Kader and De Koning, Tom J. LU
- publishing date
- 2009-11-01
- type
- Contribution to journal
- publication status
- published
- subject
- keywords
- 3-phosphoglycerate dehydrogenase deficiency, Congenital microcephaly, Drug-resistant seizures, L-serine deficiency syndromes, L-serine supplementation
- in
- Turkish Journal of Pediatrics
- volume
- 51
- issue
- 6
- pages
- 6 pages
- publisher
- Turkish National Pediatric Society
- external identifiers
-
- pmid:20196394
- scopus:76649102412
- ISSN
- 0041-4301
- language
- English
- LU publication?
- no
- id
- 623836f1-135b-45b9-a0bd-01c5a13ab1e8
- date added to LUP
- 2020-02-28 13:49:22
- date last changed
- 2025-04-04 15:03:05
@article{623836f1-135b-45b9-a0bd-01c5a13ab1e8, abstract = {{<p>Serine deficiency disorders are a new group of neurometabolic diseases resulting from a deficiency in one of the three enzymes in the biosynthetic pathway of L-serine. Deficiency of the enzyme 3-phosphoglycerate dehydrogenase (3-PGDH), which catalyzes the first step in the biosynthetic pathway, leads to congenital microcephaly, severe psychomotor retardation, and intractable seizures. We report a 4 1/2-year-old boy who presented with congenital microcephaly, psychomotor retardation, hypertonia, strabismus, and drug-resistant seizures due to 3-PGDH deficiency. His seizures responded to L-serine and glycine supplementation only. This potentially treatable disease should be borne in mind in patients with congenital microcephaly, psychomotor retardation and seizures. A timely diagnosis based on the detection of low cerebrospinal fluid levels of L-serine and glycine is expected to further increase the success of L-serine and glycine supplementation in these patients.</p>}}, author = {{Coşkun, Turgay and Aydin, Halil Ibrahim and Kiliç, Mustafa and Dursun, Ali and Haliloǧlu, Göknur and Topaloǧlu, Haluk and Karli-Oǧuz, Kader and De Koning, Tom J.}}, issn = {{0041-4301}}, keywords = {{3-phosphoglycerate dehydrogenase deficiency; Congenital microcephaly; Drug-resistant seizures; L-serine deficiency syndromes; L-serine supplementation}}, language = {{eng}}, month = {{11}}, number = {{6}}, pages = {{587--592}}, publisher = {{Turkish National Pediatric Society}}, series = {{Turkish Journal of Pediatrics}}, title = {{3-phosphoglycerate dehydrogenase deficiency : A case report of a treatable cause of seizures}}, volume = {{51}}, year = {{2009}}, }