PARKIN protein-deficient iPSC line (FINi006-A) from an early-onset Parkinson's disease female patient
(2025) In Stem Cell Research 87.- Abstract
Compound heterozygosity for strong hypomorphic mutations in the PRKN gene is a common cause of autosomal familial Parkinson's disease (PD). We generated an iPSC cell line from the fibroblasts of a PARKIN protein-deficient early-onset PD female patient, carrying genomic deletions of exon 2 and exons 5–7. This line displays characteristic human iPSC morphology and expression of pluripotency-associated genes, and the ability to differentiate into derivatives of three embryonic germ layers, and has a normal karyotype without any SNP array-detectable copy number variations. We anticipate the value of this PARKIN-deficient iPSC line and its derivatives in illuminating the intracellular role of this protein, contributing to the development of... (More)
Compound heterozygosity for strong hypomorphic mutations in the PRKN gene is a common cause of autosomal familial Parkinson's disease (PD). We generated an iPSC cell line from the fibroblasts of a PARKIN protein-deficient early-onset PD female patient, carrying genomic deletions of exon 2 and exons 5–7. This line displays characteristic human iPSC morphology and expression of pluripotency-associated genes, and the ability to differentiate into derivatives of three embryonic germ layers, and has a normal karyotype without any SNP array-detectable copy number variations. We anticipate the value of this PARKIN-deficient iPSC line and its derivatives in illuminating the intracellular role of this protein, contributing to the development of PD.
(Less)
- author
- organization
- publishing date
- 2025-09
- type
- Contribution to journal
- publication status
- published
- subject
- in
- Stem Cell Research
- volume
- 87
- article number
- 103795
- publisher
- Elsevier
- external identifiers
-
- scopus:105012130120
- pmid:40749621
- ISSN
- 1873-5061
- DOI
- 10.1016/j.scr.2025.103795
- language
- English
- LU publication?
- yes
- additional info
- Publisher Copyright: © 2025
- id
- 8fc1b8d1-2679-4323-aa17-4b43de71ce20
- date added to LUP
- 2025-11-20 14:33:10
- date last changed
- 2025-11-20 14:34:06
@article{8fc1b8d1-2679-4323-aa17-4b43de71ce20,
abstract = {{<p>Compound heterozygosity for strong hypomorphic mutations in the PRKN gene is a common cause of autosomal familial Parkinson's disease (PD). We generated an iPSC cell line from the fibroblasts of a PARKIN protein-deficient early-onset PD female patient, carrying genomic deletions of exon 2 and exons 5–7. This line displays characteristic human iPSC morphology and expression of pluripotency-associated genes, and the ability to differentiate into derivatives of three embryonic germ layers, and has a normal karyotype without any SNP array-detectable copy number variations. We anticipate the value of this PARKIN-deficient iPSC line and its derivatives in illuminating the intracellular role of this protein, contributing to the development of PD.</p>}},
author = {{Pavan, Chiara and Jin, Jennifer and Jong, Sharon and Qian, Gordon and Strbenac, Dario and Davis, Ryan L. and Halliday, Glenda M. and Kirik, Deniz and Parish, Clare L. and Thompson, Lachlan H. and Sue, Carolyn M. and Ovchinnikov, Dmitry A.}},
issn = {{1873-5061}},
language = {{eng}},
publisher = {{Elsevier}},
series = {{Stem Cell Research}},
title = {{PARKIN protein-deficient iPSC line (FINi006-A) from an early-onset Parkinson's disease female patient}},
url = {{http://dx.doi.org/10.1016/j.scr.2025.103795}},
doi = {{10.1016/j.scr.2025.103795}},
volume = {{87}},
year = {{2025}},
}
