1 – 21 of 21
- show: 100
- |
- sort: year (new to old)
Close
Embed this list
<iframe src=" "
width=" "
height=" "
allowtransparency="true"
frameborder="0">
</iframe>
- 2011
-
Mark
Mice with ribosomal protein S19 deficiency develop bone marrow failure and symptoms like patients with Diamond-Blackfan anemia.
(
- Contribution to journal › Article
- 2009
-
Mark
Development of Novel Therapies in Murine Models for Gaucher Disease
(
- Chapter in Book/Report/Conference proceeding › Paper in conference proceeding
-
Mark
Successful Low-Risk Hematopoietic Cell Therapy in a Mouse Model of Type 1 Gaucher Disease
(
- Contribution to journal › Article
- 2008
-
Mark
RPS19 Deficiency Leads to Reduced Proliferation and Increased Apoptosis but Does Not Affect Terminal Erythroid Differentiation in a Cell Line Model of Diamond-Blackfan Anemia
(
- Contribution to journal › Article
-
Mark
Gene therapy of Diamond Blackfan anemia CD34(+) cells leads to improved erythroid development and engraftment following transplantation.
(
- Contribution to journal › Article
-
Mark
Successful low-risk hematopoietic cell therapy in a mouse model of type 1 Gaucher disease.
2008) p.1189-1190(
- Contribution to conference › Poster
- 2007
-
Mark
Murine models of acute neuronopathic Gaucher disease
(
- Contribution to journal › Article
-
Mark
Hematopoietic stem cell targeted neonatal gene therapy reverses lethally progressive osteopetrosis in oc/oc mice.
(
- Contribution to journal › Article
- 2006
-
Mark
Effective cell and gene therapy in a murine model of Gaucher disease.
(
- Contribution to journal › Article
-
Mark
Neonatal hematopoietic stem cell transplantation cures oc/oc mice from osteopetrosis.
(
- Contribution to journal › Article
- 2005
-
Mark
Development of cellular models for ribosomal protein S19 (RPS19)-deficient diamond-blackfan anemia using inducible expression of siRNA against RPS19.
(
- Contribution to journal › Article
-
Mark
Deficiency of ribosomal protein S19 in CD34+ cells generated by siRNA blocks erythroid development and mimics defects seen in Diamond-Blackfan anemia.
(
- Contribution to journal › Article
- 2004
-
Mark
Development of an adenoviral vector system with adenovirus serotype 35 tropism; efficient transient gene transfer into primary malignant hematopoietic cells.
(
- Contribution to journal › Article
- 2003
-
Mark
Proliferation deficiency of multipotent hematopoietic progenitors in ribosomal protein S19 (RPS19)-deficient Diamond-Blackfan anemia improves following RPS19 gene transfer
(
- Contribution to journal › Article
-
Mark
Bakslag for genterapi: två fall av leukemi i fransk studie [Setback for gene therapy: Two cases of leukemia in a French trial]
(
- Contribution to journal › Article
- 2002
-
Mark
Oncoretroviral gene transfer to NOD/SCID repopulating cells using three different viral envelopes
(
- Contribution to journal › Article
-
Mark
Gene transfer improves erythroid development in ribosomal protein S19-deficient Diamond-Blackfan anemia.
(
- Contribution to journal › Article
-
Mark
Framgangsrik genterapi av barn med svar immundefekt. Forskningsgenombrott ger hopp om behandling aven av andra sjukdomar
(
- Contribution to journal › Article
- 2001
-
Mark
Clinical gene therapy in hematology: Past and future
(
- Contribution to journal › Article
-
Mark
Retroviral transduction of human CD34+ cells on fibronectin fragment CH-296 is inhibited by high concentrations of vector containing medium
(
- Contribution to journal › Article
- 2000
-
Mark
Low level of gene transfer to and engraftment of murine bone marrow cells from long-term bone marrow cultures
(
- Contribution to journal › Article