Development and Characterization of a High-Affinity Selective Galectin-3 Mouse Tool Compound in Mouse Models of Cancer
(2024) In Journal of Medicinal Chemistry 67(24). p.21905-21915- Abstract
The interest in galectin-3 as a drug target in the cancer and fibrosis space has grown during the past few years with several new classes of compounds being developed. The first orally available galectin-3 inhibitor, GB1211 (h-galectin-3 Kd = 0.025 μM), is currently in phase 2 clinical trials. Due to structural differences between human and mouse galectin-3 a significant reduction in mouse galectin-3 affinity is observed for most highly potent human galectin-3 inhibitors including GB1211 (m-galectin-3 Kd = 0.77 μM). Pharmacokinetic experiments in mouse dosing GB1211 up to 100 mg/kg results in free plasma levels below m-galectin-3 Kd, which is not comparable to the data observed in humans. To better... (More)
The interest in galectin-3 as a drug target in the cancer and fibrosis space has grown during the past few years with several new classes of compounds being developed. The first orally available galectin-3 inhibitor, GB1211 (h-galectin-3 Kd = 0.025 μM), is currently in phase 2 clinical trials. Due to structural differences between human and mouse galectin-3 a significant reduction in mouse galectin-3 affinity is observed for most highly potent human galectin-3 inhibitors including GB1211 (m-galectin-3 Kd = 0.77 μM). Pharmacokinetic experiments in mouse dosing GB1211 up to 100 mg/kg results in free plasma levels below m-galectin-3 Kd, which is not comparable to the data observed in humans. To better support translation into clinical studies, a new improved mouse galectin-3 tool compound, GB2095, was developed. Dosing this new compound in in vivo syngeneic mouse models of cancer resulted in reduction of the growth of breast and melanoma cancers.
(Less)
- author
- organization
- publishing date
- 2024
- type
- Contribution to journal
- publication status
- published
- subject
- in
- Journal of Medicinal Chemistry
- volume
- 67
- issue
- 24
- pages
- 21905 - 21915
- publisher
- The American Chemical Society (ACS)
- external identifiers
-
- scopus:85212110459
- pmid:39668131
- ISSN
- 1520-4804
- DOI
- 10.1021/acs.jmedchem.4c01747
- language
- English
- LU publication?
- yes
- id
- facb966d-64d7-4608-8194-42918f1da2ae
- date added to LUP
- 2024-12-19 18:58:16
- date last changed
- 2025-08-01 22:56:00
@article{facb966d-64d7-4608-8194-42918f1da2ae, abstract = {{<p>The interest in galectin-3 as a drug target in the cancer and fibrosis space has grown during the past few years with several new classes of compounds being developed. The first orally available galectin-3 inhibitor, GB1211 (h-galectin-3 K<sub>d</sub> = 0.025 μM), is currently in phase 2 clinical trials. Due to structural differences between human and mouse galectin-3 a significant reduction in mouse galectin-3 affinity is observed for most highly potent human galectin-3 inhibitors including GB1211 (m-galectin-3 K<sub>d</sub> = 0.77 μM). Pharmacokinetic experiments in mouse dosing GB1211 up to 100 mg/kg results in free plasma levels below m-galectin-3 K<sub>d</sub>, which is not comparable to the data observed in humans. To better support translation into clinical studies, a new improved mouse galectin-3 tool compound, GB2095, was developed. Dosing this new compound in in vivo syngeneic mouse models of cancer resulted in reduction of the growth of breast and melanoma cancers. </p>}}, author = {{Peterson, Kristoffer and Nilsson, Ulf J. and Gravelle, Lise and Holyer, Ian and Jansson, Karl and Kahl-Knutson, Barbro and Leffler, Hakon and MacKinnon, Alison C. and Roper, James A. and Slack, Robert J. and von Wachenfeldt, Henrik and Pedersen, Anders and Zetterberg, Fredrik R.}}, issn = {{1520-4804}}, language = {{eng}}, number = {{24}}, pages = {{21905--21915}}, publisher = {{The American Chemical Society (ACS)}}, series = {{Journal of Medicinal Chemistry}}, title = {{Development and Characterization of a High-Affinity Selective Galectin-3 Mouse Tool Compound in Mouse Models of Cancer}}, url = {{http://dx.doi.org/10.1021/acs.jmedchem.4c01747}}, doi = {{10.1021/acs.jmedchem.4c01747}}, volume = {{67}}, year = {{2024}}, }