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- 2024
-
Mark
Preventive cognitive protection based on AAV9 overexpression of IGF1 in hippocampal astrocytes
(
- Contribution to journal › Article
-
Mark
Newborn screening in metachromatic leukodystrophy – European consensus-based recommendations on clinical management
(
- Contribution to journal › Article
-
Mark
Age-related disease : Cardiovascular system
2024) p.35-52(
- Chapter in Book/Report/Conference proceeding › Book chapter
- 2023
-
Mark
Precision mapping of gene expression and proteins in the brain using gene editing and barcoded viral vectors
2023) In Lund University, Faculty of Medicine Doctoral Dissertation Series(
- Thesis › Doctoral thesis (compilation)
-
Mark
Optogenetics for controlling seizure circuits for translational approaches
(
- Contribution to journal › Article
-
Mark
Infrastructural considerations of implementing gene therapy for hemophilia in the Nordic context
(
- Contribution to journal › Article
- 2022
-
Mark
Enhancing neuronal inhibition by cell and gene therapy as a novel treatment for Epilepsy
2022) In Lund University, Faculty of Medicine Doctoral Dissertation Series(
- Thesis › Doctoral thesis (compilation)
-
Mark
Alternative payment models for durable and potentially curative therapies : The case of gene therapy for haemophilia A
(
- Contribution to journal › Article
-
Mark
Development and Characterisation of a Rat Model of Parkinson's Disease
2022) In Lund University, Faculty of Medicine Doctoral Dissertation Series(
- Thesis › Doctoral thesis (compilation)
-
Mark
Editorial : Gene therapy 2.0: Biotechnology for circuit engineering and complex therapeutic approaches
(
- Contribution to journal › Debate/Note/Editorial
- 2021
-
Mark
Toward a New Paradigm for Targeted Natriuretic Peptide Enhancement in Heart Failure
(
- Contribution to journal › Scientific review
-
Mark
Editorial : Gene Therapy in the CNS – Progress and Prospects for Novel Therapies
(
- Contribution to journal › Debate/Note/Editorial
-
Mark
Gene therapy for infantile malignant osteopetrosis : review of pre-clinical research and proof-of-concept for phenotypic reversal
(
- Contribution to journal › Scientific review
- 2020
-
Mark
Late presentation of RPE65 retinopathy in three siblings
(
- Contribution to journal › Article
-
Mark
Advancing gene therapy for epilepsy. Translational pre-clinical studies with neuropeptide Y and glial cell-line derived neurotrophic factor.
2020) In Lund University, Faculty of Medicine Doctoral Dissertation Series(
- Thesis › Doctoral thesis (compilation)
-
Mark
Gene Therapy Vector Encoding Neuropeptide Y and Its Receptor Y2 for Future Treatment of Epilepsy : Preclinical Data in Rats
(
- Contribution to journal › Article
-
Mark
Development and Validation of CRISPR Activator Systems for Overexpression of CB1 Receptors in Neurons
(
- Contribution to journal › Article
-
Mark
AAV Production Everywhere : A Simple, Fast, and Reliable Protocol for In-house AAV Vector Production Based on Chloroform Extraction
(
- Contribution to journal › Article
- 2019
-
Mark
Practical Considerations for the Use of DREADD and Other Chemogenetic Receptors to Regulate Neuronal Activity in the Mammalian Brain
(
- Contribution to journal › Article
- 2018
-
Mark
Retinal AAV8-RS1 Gene Therapy for X-Linked Retinoschisis : Initial Findings from a Phase I/IIa Trial by Intravitreal Delivery
(
- Contribution to journal › Article
-
Mark
Development of Novel Therapies, Models, and Biomarkers for Osteoclast-Related Diseases
(
- Thesis › Doctoral thesis (compilation)
-
Mark
Destabilizing Domains Enable Long-Term and Inert Regulation of GDNF Expression in the Brain
(
- Contribution to journal › Article
-
Mark
Haemophilia B : Where are we now and what does the future hold?
(
- Contribution to journal › Scientific review
- 2017
-
Mark
Lentiviral Vectors with Cellular Promoters Correct Anemia and Lethal Bone Marrow Failure in a Mouse Model for Diamond-Blackfan Anemia
(
- Contribution to journal › Article
-
Mark
Rearing light intensity affects inner retinal pathology in a mouse model of x-linked retinoschisis but does not alter gene therapy outcome
(
- Contribution to journal › Article
-
Mark
The clinical phenotype of CNGA3-related achromatopsia : Pretreatment characterization in preparation of a gene replacement therapy trial
(
- Contribution to journal › Article
- 2016
-
Mark
Regulation and Function of Lentiviral Vector-Mediated TCIRG1 Expression in Osteoclasts from Patients with Infantile Malignant Osteopetrosis : Implications for Gene Therapy
(
- Contribution to journal › Article
- 2015
-
Mark
Cell and gene therapy for blood disorders. Modeling of novel treatment strategies for Gaucher type 1 disease and Diamond-Blackfan anemia in mice.
(
- Thesis › Doctoral thesis (compilation)
-
Mark
Non-Viral Deoxyribonucleoside Kinases - Diversity and Practical Use
(
- Contribution to journal › Scientific review
- 2014
-
Mark
Development of Novel Models for Studying Osteoclasts
(
- Thesis › Doctoral thesis (compilation)
-
Mark
Factor VIII therapy for hemophilia A: current and future issues
(
- Contribution to journal › Scientific review
- 2013
-
Mark
Neuropeptides and neurotrophic factors in epilepsy: seizure suppressant actions of VEGF, NPY and galanin
(
- Thesis › Doctoral thesis (compilation)
- 2012
-
Mark
Targeting the hematopoietic stem cell to correct osteopetrosis
(
- Thesis › Doctoral thesis (compilation)
-
Mark
How can measurement, monitoring, modeling and control advance cell culture in industrial biotechnology?
(
- Contribution to journal › Article
-
Mark
Novel disease-specific promoters for use in gene therapy for Parkinson's disease.
(
- Contribution to journal › Article
-
Mark
Combined gene overexpression of neuropeptide Y and its receptor Y5 in the hippocampus suppresses seizures
(
- Contribution to journal › Article
- 2011
-
Mark
Stem cell self-renewal: lessons from bone marrow, gut and iPS toward clinical applications
(
- Contribution to journal › Scientific review
-
Mark
Inclusion of a single-tail amino acid-based amphiphile in a lipoplex formulation: Effects on transfection efficiency and physicochemical properties
(
- Contribution to journal › Article
- 2010
-
Mark
Gene therapy in a new model of delayed wound healing
(
- Thesis › Doctoral thesis (compilation)
-
Mark
Gene Therapy for Neurological Disorders
(
- Thesis › Doctoral thesis (compilation)
-
Mark
X-LINKED RETINOSCHISIS ELECTROPHYSIOLOGY, MOLECULAR GENETICS AND TREATMENT
(
- Thesis › Doctoral thesis (compilation)
-
Mark
New strategies for plasmid DNA purification using aqueous two phase systems and multimodal chromatography
2010) 14th International Biotechnology Symposium and Exhibition (IBS-2008) In Journal of Biotechnology 150(Suppl. 1). p.186-186(
- Contribution to journal › Published meeting abstract
-
Mark
Transgenic overexpression of laminin 1 chain in laminin 2 chain-deficient mice rescues the disease throughout the lifespan
(
- Contribution to journal › Article
-
Mark
Gene therapy and enhancement for diabetes (and other diseases) : The multiplicity of considerations
(
- Contribution to journal › Scientific review
- 2009
-
Mark
Characterization of Meteorin-An Evolutionary Conserved Neurotrophic Factor
(
- Contribution to journal › Article
-
Mark
Assessment of CAR- or CD46-Dependent Adenoviral Vector-Mediated TRAIL Gene Therapy in Clinical Adenocarcinoma Lung Cancer Cells
(
- Contribution to journal › Article
-
Mark
Neuron-specific RNA interference using lentiviral vectors
(
- Contribution to journal › Article
-
Mark
Bacterial Deoxyribonucleoside Kinases Are Poor Suicide Genes in Mammalian Cells
(
- Contribution to journal › Article
-
Mark
Gene therapy by enzyme replacement for Parkinson’s disease Optimization of continuous DOPA delivery and development of a candidate vector for clinical application
(
- Thesis › Doctoral thesis (compilation)
-
Mark
Deoxyribonucleoside kinases in bacteria, plants and humans
2009)(
- Thesis › Doctoral thesis (compilation)