Division of Molecular Medicine and Gene Therapy
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- 2009
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Mark
Fetal Gene Therapy for Acute Neuronopathic Gaucher Disease
2009) 12th Annual Meeting of the American Society of Gene Therapy In Molecular Therapy 17. p.357-357(
- Contribution to journal › Published meeting abstract
-
Mark
Lipocalin 2 negatively controls erythroid and macrophage lineages via megalin as its receptor
2009) 38th Annual Scientific Meeting of the ISEH-Society-for-Hematology-and-Stem-Cells In Experimental Hematology 37(9). p.80-81(
- Contribution to journal › Published meeting abstract
-
Mark
Development of Novel Therapies in Murine Models for Gaucher Disease
(
- Chapter in Book/Report/Conference proceeding › Paper in conference proceeding
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Mark
THE ROLE OF BMP SIGNALING AND ENDOGLIN IN REGULATION OF HEMATOPOIESIS
(
- Thesis › Doctoral thesis (compilation)
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Mark
Successful Low-Risk Hematopoietic Cell Therapy in a Mouse Model of Type 1 Gaucher Disease
(
- Contribution to journal › Article
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Mark
Development of Mouse Models and Gene Therapy for Gaucher Disease
(
- Thesis › Doctoral thesis (compilation)
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Mark
Neonatal bone marrow transplantation without prior conditioning rapidly reverses osteopetrosis in oc/oc mice despite only minimal donor cell engraftment
(
- Contribution to journal › Published meeting abstract
-
Mark
SMAD4 as a therapeutic target in hoxa9-related leukemia
2009) 38th Annual Scientific Meeting of the ISEH-Society-for-Hematology-and-Stem-Cells In Experimental Hematology 37(9). p.44-45(
- Contribution to journal › Published meeting abstract
-
Mark
No evidence for activation of the unfolded protein response in neuronopathic models of Gaucher disease
(
- Contribution to journal › Article
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Mark
Low-dose busulphan conditioning and neonatal stem cell transplantation preserves vision and restores hematopoiesis in severe murine osteopetrosis.
(
- Contribution to journal › Article
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Mark
Complex and context dependent regulation of hematopoiesis by TGF-beta superfamily signaling.
(
- Contribution to journal › Scientific review
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Mark
Is TGF-beta a stemness regulator?
(
- Contribution to journal › Article
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Mark
Hematopoietic Cell-Specific Deletion of Toll-like Receptor 4 Ameliorates Hepatic and Adipose Tissue Insulin Resistance in High-Fat-Fed Mice
(
- Contribution to journal › Article
-
Mark
Prospects for gene therapy of osteopetrosis.
(
- Contribution to journal › Article
- 2008
-
Mark
Diagnosing and treating Diamond Blackfan anaemia: results of an international clinical consensus conference
(
- Contribution to journal › Scientific review
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Mark
Neonatal hematopoietic stem cell transplantation following low-dose busulphan conditioning reverses osteopetrosis and preserves vision in oc/oc mice
2008) 16th Annual Congress of the European-Society-of-Gene-and-Cell-Therapy In Human Gene Therapy 19(10). p.1183-1184(
- Contribution to journal › Published meeting abstract
-
Mark
Hematopoietic stem cell responsiveness to exogenous signals is limited by Caspase-3
(
- Contribution to journal › Article
-
Mark
A critical role for Smad4 in the self-renewal of hematopoietic stem cells
2008) 4th Conference on Stem Cell Gene Therapy In Blood Cells, Molecules, and Diseases 40(2). p.271-271(
- Contribution to journal › Published meeting abstract
-
Mark
Brain area-specific effect of TGF-beta signaling on Wnt-dependent neural stem cell expansion
(
- Contribution to journal › Article
-
Mark
Enforced expression of c-Ski in adult murine hematopoiesis promotes myeloid - Differentiation, revealing an important role for c-Ski in governing hematopoietic cell fate options
2008) 37th Annual Scientific Meeting featuring the 6th International Neonatal Hematology and Immunology Meeting In Experimental Hematology 36(7, Supplement 1). p.29-29(
- Contribution to journal › Published meeting abstract
-
Mark
W41/w41 blastocyst complementation: A versatile system to study gene function in hematopotetic stem cells
2008) 37th Annual Scientific Meeting featuring the 6th International Neonatal Hematology and Immunology Meeting In Experimental Hematology 36(7, Supplement 1). p.67-68(
- Contribution to journal › Published meeting abstract
-
Mark
W41/W41 blastocyst complementation: A versatile system to study gene function in hematopoietic stem cells
2008) 37th Annual Scientific Meeting featuring the 6th International Neonatal Hematology and Immunology Meeting In Experimental Hematology 36(7, Supplement 1). p.5-5(
- Contribution to journal › Published meeting abstract
-
Mark
A HOXA10-inducible mouse model demonstrates an important role of the initial transforming event in the maintenance of the leukemia
2008) 37th Annual Scientific Meeting featuring the 6th International Neonatal Hematology and Immunology Meeting In Experimental Hematology 36(7, Supplement 1). p.4-5(
- Contribution to journal › Published meeting abstract
-
Mark
Therapeutic effects of bone marrow transplantation for metachromatic leukodystrophy using HOXB4 over-expressing cells
2008) The 13th Annual Meeting 2007 Japan Society of Gene Therapy In Journal of Gene Medicine 10(4). p.476-477(
- Contribution to journal › Published meeting abstract
-
Mark
Clonal mar-king and genetic manipulation of AGM HSCs
2008) 37th Annual Scientific Meeting featuring the 6th International Neonatal Hematology and Immunology Meeting In Experimental Hematology 36(7, Supplement 1). p.69-69(
- Contribution to journal › Published meeting abstract
-
Mark
Signaling via the Tgf-beta type I receptor Alk5 in heart development
(
- Contribution to journal › Article
-
Mark
Smad4 as a Therapeutic Target in Nup98-HoxA9-Induced Leukemia.
(
- Contribution to journal › Published meeting abstract
-
Mark
RPS19 Deficiency Leads to Reduced Proliferation and Increased Apoptosis but Does Not Affect Terminal Erythroid Differentiation in a Cell Line Model of Diamond-Blackfan Anemia
(
- Contribution to journal › Article
-
Mark
Human Primary Mensenchymal Stromal Progenitor Cells Are Highly Enriched in Both, the CD271(+)/CD146(+) and CD271(+)/CD146(-) Bone Marrow Population with the Latter Acquiring CD146 Expression upon Culture in-Vitro.
(
- Contribution to journal › Published meeting abstract
-
Mark
Towards a better understanding and new therapeutics of osteopetrosis.
(
- Contribution to journal › Scientific review
-
Mark
Gene therapy of Diamond Blackfan anemia CD34(+) cells leads to improved erythroid development and engraftment following transplantation.
(
- Contribution to journal › Article
-
Mark
Successful low-risk hematopoietic cell therapy in a mouse model of type 1 Gaucher disease.
2008) p.1189-1190(
- Contribution to conference › Poster
-
Mark
Stem cell regulation and host defense: the logic and the paradox.
(
- Contribution to journal › Article
-
Mark
Delection of the SCN gene cluster on 2q24.4 is associated with severe epilepsy an array-based genotype-phenotype correlation and a comprehensive review of previously published area
(
- Contribution to journal › Article
-
Mark
Signaling pathways governing stem cell fate.
(
- Contribution to journal › Scientific review
- 2007
-
Mark
Fusion gene-mediated truncation of RUNX1 as a potential mechanism underlying disease progression in the 8p11 myeloproliferative syndrome.
(
- Contribution to journal › Article
-
Mark
Hematopoietic stem cell targeted neonatal gene therapy reverses lethally progressive osteopetrosis in oc/oc mice.
(
- Contribution to journal › Article
-
Mark
Female mice are more susceptible to developing inflammatory disorders due to impaired transforming growth factor beta signaling in salivary glands
(
- Contribution to journal › Article
-
Mark
Hoxa9/hoxb3/hoxb4 compound null mice display severe hematopoietic defects
(
- Contribution to journal › Article
-
Mark
Murine models of acute neuronopathic Gaucher disease
(
- Contribution to journal › Article
-
Mark
Adenoviral vectors for transient gene expression in human primitive hematopoietic cells: Applications and prospects.
(
- Contribution to journal › Scientific review
-
Mark
TGF-beta receptor I conditional knockout mice develop spontaneous squamous cell carcinoma
(
- Contribution to journal › Article
-
Mark
Diamond-Blackfan anemia: erythropoiesis lost in translation.
(
- Contribution to journal › Scientific review
-
Mark
HOXA10 is a critical regulator for hematopoietic stem cells and erythroid/megakaryocyte development.
(
- Contribution to journal › Article
-
Mark
Ectopic expression of PAX5 promotes self renewal of bi-phenotypic myeloid progenitors co-expressing myeloid and B-cell lineage associated genes.
(
- Contribution to journal › Article
-
Mark
Alpha10 integrin expression is up-regulated on fibroblast growth factor-2-treated mesenchymal stem cells with improved chondrogenic differentiation potential.
(
- Contribution to journal › Article
-
Mark
Connecting ribosomes with bone marrow failure
(
- Contribution to journal › Debate/Note/Editorial
-
Mark
Neuron-specific TGF-beta signaling deficiency results in retinal detachment and cataracts in mice
(
- Contribution to journal › Article
-
Mark
Human RPS19, the gene mutated in Diamond Blackfan anemia, encodes a ribosomal protein required for the maturation of 40S ribosomal subunits.
(
- Contribution to journal › Article
-
Mark
Temporal trends of esophageal cancer during 1995-2004 in Nanao Island, an extremely high-risk area in China
(
- Contribution to journal › Article
-
Mark
Towards Gene Therapy of Osteopetrosis.
2007)(
- Thesis › Doctoral thesis (compilation)
-
Mark
Glioma stem cells: Evidence and limitation.
(
- Contribution to journal › Scientific review
-
Mark
Smad4 is critical for self-renewal of hematopoietic stem cells.
(
- Contribution to journal › Article
-
Mark
Repopulation of adult and neonatal mice with human hepatocytes : A chimeric animal model
2007) In Proceedings of the National Academy of Sciences of the United States of America 104(51). p.20507-20511(
- Contribution to journal › Article
-
Mark
Genetic intratumour heterogeneity in high-grade brain tumours is associated with telomere-dependent mitotic instability.
(
- Contribution to journal › Article
-
Mark
Smad signaling in hematopoietic stem cell biology
2007)(
- Thesis › Doctoral thesis (compilation)
-
Mark
The Role of Hox Transcription Factors in the Regulation of Hematopoiesis
2007) In 2007:26(
- Thesis › Doctoral thesis (compilation)
-
Mark
Diamond-Blackfan Anemia: Erythropoiesis Lost in Translation
2007)(
- Thesis › Doctoral thesis (compilation)
-
Mark
Adenoviruses Use Lactoferrin as a Bridge for CAR-Independent Binding to and Infection of Epithelial Cells.
(
- Contribution to journal › Article
-
Mark
Endoglin is not critical for hematopoietic stem cell engraftment and reconstitution but regulates adult erythroid development
(
- Contribution to journal › Article
- 2006
-
Mark
Human short-term repopulating cells have enhanced telomerase reverse transcriptase expression.
(
- Contribution to journal › Article
-
Mark
Distribution of vesicular glutamate transporters 1 and 2 in the rat spinal cord, with a note on the spinocervical tract.
(
- Contribution to journal › Article
-
Mark
Erythropoiesis in the Rps19 disrupted mouse: Analysis of erythropoietin response and biochemical markers for Diamond-Blackfan anemia
(
- Contribution to journal › Article
-
Mark
Epithelial and ectomesenchymal role of the type I TGF-beta receptor ALK5 during facial morphogenesis and palatal fusion
(
- Contribution to journal › Article
-
Mark
Smad7 promotes self-renewal of hematopoietic stem cells in vivo.
(
- Contribution to journal › Article
-
Mark
Neonatal hematopoietic stem cell transplantation cures oc/oc mice from osteopetrosis.
(
- Contribution to journal › Article
-
Mark
Effective cell and gene therapy in a murine model of Gaucher disease.
(
- Contribution to journal › Article
-
Mark
Smad5 is dispensable for adult murine hematopoiesis.
(
- Contribution to journal › Article
-
Mark
Detection of cell cycle- and differentiation stage-dependent human telomerase reverse transcriptase expression in single living cancer cells.
(
- Contribution to journal › Article
-
Mark
Increased expression of cyclin A1 protein is associated with all-trans retinoic acid-induced apoptosis.
(
- Contribution to journal › Article
-
Mark
A road map towards defining the role of Smad signaling in hematopoietic stem cells.
(
- Contribution to journal › Article
-
Mark
Cell type- and region- dependent coxsackie adenovirus receptor expression in the central nervous system.
(
- Contribution to journal › Article
-
Mark
Regulation of hematopoiesis by the Smad signaling pathway
2006)(
- Thesis › Doctoral thesis (compilation)
-
Mark
A critical developmental role for tgfbr2 in myogenic cell lineages is revealed in mice expressing SM22-Cre, not SMMHC-Cre
(
- Contribution to journal › Article
-
Mark
HOXB4-induced self-renewal of hematopoietic stem cells is significantly enhanced by p21 deficiency.
(
- Contribution to journal › Article
-
Mark
Defective ALK5 signaling in the neural crest leads to increased postmigratory neural crest cell apoptosis and severe outflow tract defects
(
- Contribution to journal › Article
- 2005
-
Mark
Quiescence of hematopoietic stem cells and maintenance of the stem cell pool is not dependent on TGF-beta signaling in vivo.
(
- Contribution to journal › Article
-
Mark
Identification of conserved amino acids N-terminal of the PKCeC1bdomain crucial for PKCe-mediated induction of neurite outgrowth.
(
- Contribution to journal › Article
-
Mark
DNA-binding dependent and independent functions of WT1 protein during human hematopoiesis.
(
- Contribution to journal › Article
-
Mark
Bone-marrow-derived cells contribute to the recruitment of microglial cells in response to beta-amyloid deposition in APP/PS1 double transgenic Alzheimer mice
(
- Contribution to journal › Article
-
Mark
Gene Transfer to Repopulating Human CD34(+) Cells Using Amphotropic-, GALV-, or RD114-Pseudotyped HIV-1-Based Vectors from Stable Producer Cells.
(
- Contribution to journal › Article
-
Mark
Culturing of human tumor cells for use in immune gene tumor therapy
2005) World Federation of Neuro-Oncology Second Quadrennial Meeting and the Sixth Meeting of the European Association for Neuro-Oncology In Neuro-Oncology 7(3). p.371-371(
- Contribution to journal › Published meeting abstract
-
Mark
Expression of cyclin A1 and cell cycle proteins in hematopoietic cells and acute myeloid leukemia and links to patient outcome.
(
- Contribution to journal › Article
-
Mark
Development of cellular models for ribosomal protein S19 (RPS19)-deficient diamond-blackfan anemia using inducible expression of siRNA against RPS19.
(
- Contribution to journal › Article
-
Mark
Compound developmental eye disorders following inactivation of TGFbeta signaling in neural-crest stem cells
(
- Contribution to journal › Article
-
Mark
TGF-{beta} type II receptor deficient thymocytes develop normally but demonstrate increased CD8+ proliferation in vivo.
(
- Contribution to journal › Article
-
Mark
Gene therapy: efficient targeting of hematopoietic stem cells
(
- Contribution to journal › Debate/Note/Editorial
-
Mark
Deficiency of ribosomal protein S19 in CD34+ cells generated by siRNA blocks erythroid development and mimics defects seen in Diamond-Blackfan anemia.
(
- Contribution to journal › Article
-
Mark
The role of Smad signaling in hematopoiesis.
(
- Contribution to journal › Scientific review
-
Mark
Altered primordial germ cell migration in the absence of transforming growth factor beta signaling via ALK5
(
- Contribution to journal › Article
-
Mark
Gene expression profiling demonstrates that TGF-{beta}1 signals exclusively through receptor complexes involving Alk5 and identifies targets of TGF-{beta} signaling.
(
- Contribution to journal › Article
-
Mark
Inactivation of TGF beta signaling in neural crest stem cells leads to multiple defects reminiscent of DiGeorge syndrome
(
- Contribution to journal › Article
-
Mark
Human immunodeficiency virus type 1 vectors with alphavirus envelope glycoproteins produced from stable packaging cells
(
- Contribution to journal › Article
-
Mark
Candesartan prevents angiotensin II-induced facilitation of hypoxic neuronal damage through PKC delta inhibition
(
- Contribution to journal › Article
- 2004
-
Mark
Connective tissue growth factor expression and Smad signaling during mouse heart development and myocardial infarction
(
- Contribution to journal › Article
-
Mark
Defective paracrine signalling by TGF beta in yolk sac vasculature of endoglin mutant mice: a paradigm for hereditary haemorrhagic telangiectasia
(
- Contribution to journal › Article
-
Mark
Development of an adenoviral vector system with adenovirus serotype 35 tropism; efficient transient gene transfer into primary malignant hematopoietic cells.
(
- Contribution to journal › Article
-
Mark
Targeted disruption of the ribosomal protein S19 gene is lethal prior to implantation
(
- Contribution to journal › Article
-
Mark
Chance or necessity? Insertional mutagenesis in gene therapy and its consequences
(
- Contribution to journal › Scientific review
-
Mark
Stem cell expansion: success and complexities
(
- Contribution to journal › Debate/Note/Editorial